First gene therapy for children with metachromatic leukodystrophy approved by FDA

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First gene therapy for children with metachromatic leukodystrophy approved by FDA
United Kingdom Latest News,United Kingdom Headlines
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The U.S. Food and Drug Administration has approved Orchard Therapeutics' Lenmeldy (atidarsagene autotemcel) as the first gene therapy for the treatment of children with metachromatic leukodystrophy (MLD).

First gene therapy for children with metachromatic leukodystrophy approved by FDA retrieved 25 March 2024 from https://medicalxpress.com/news/2024-03-gene-therapy-children-metachromatic-leukodystrophy.html

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